How Does Gene Therapy Work

Scientists have promised that

Gene therapy

gene therapy works

Developed by CSL Behring, this video aims to shine a light on the science behind transformative

When we looked at some areas of biotechnology earlier in the series, we briefly touched on

Connect with a specialist: http://bit.ly/2nIxt7t Meet Jerry Mendell, MD: http://bit.ly/2nCirzT More about SMA Type 1: ...

Gene therapy

Gene therapy

Many diseases have a

Can gene therapy

Learn more: http://www.childrenshospital.org/

Although still in its early stages,

CRISPR is a powerful

What if doctors could take a child's own cells, fix them in a lab, and return them to fight disease? That's the promise of ex vivo

Explore the science of the groundbreaking technology for editing

Sickle cell disease is an inherited blood disorder that causes red blood cells to deform and become sickle (or crescent) shaped.

In the mid-1960s a small and unusual type of virus, known as AAV, was discovered. AAV cannot replicate on its own and it causes ...

Gene